Case report: first diagnosis of VEXAS Syndrome in Costa Rica

 

Gorde:
Xehetasun bibliografikoak
Egileak: Masís-Mejía, Rodrigo, Brenes-Piedra, Luis Miguel, Jiménez-Solera, María Paz, Santamaría-Quesada, Carlos, Gallegos-Mesén, Alejandra, Sánchez-Benavides, Marvin
Formatua: artículo original
Egoera:Versión publicada
Argitaratze data:2025
Deskribapena:Introduction: VEXAS syndrome (Vacuoles, E1 enzyme, X-linked, Autoinflammatory, Somatic) is an autoinflammatory condition caused by somatic mutations in the UBA1 gene on the X chromosome. Materials: We present the case of a 65-year-old male with relapsing polychondritis admitted with severe systemic inflammation, fever, deep vein thrombosis, and myelodysplasia. Infectious and rheumatologic causes were ruled out. Results: Genetic sequencing confirmed a UBA1 mutation. Conclusion: Steroid treatment led to rapid clinical improvement and decreased inflammatory parameters.
Herria:Portal de Revistas UCR
Erakundea:Universidad de Costa Rica
Repositorio:Portal de Revistas UCR
Hizkuntza:Español
OAI Identifier:oai:portal.ucr.ac.cr:article/61773
Sarrera elektronikoa:https://revistas.ucr.ac.cr/index.php/medica/article/view/61773
Gako-hitza:Síndrome VEXAS, gen UBA1, autoinflamatorio, síndrome mielodisplásico, reporte de caso
VEXAS syndrome, UBA1 gene, autoinflammatory disease, myelodysplastic syndrome, case report